Research output per year
Research output per year
Search results
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2022
Targeted exon skipping of NF1 exon 17 as a Therapeutic for Neurofibromatosis Type I
Leier, A., Moore, M., Liu, H., Daniel, M., Hyde, A. M., Messiaen, L., Korf, B. R., Selvakumaran, J., Ciszewski, L., Lambert, L., Foote, J., Wallace, M. R., Kesterson, R. A., Dickson, G., Popplewell, L. & Wallis, D., 15 Mar 2022, In: Molecular therapy. Nucleic acids.Research output: Contribution to journal › Article › peer-review
Open Access -
2021
Restoration of Normal NF1 Function with Antisense Morpholino Treatment of Recurrent Pathogenic Patient-Specific Variant c.1466A>G; p.Y489C
Awad, E., Moore, M., Liu, H., Ciszewski, L., Lambert, L., Korf, B. R., Popplewell, L., Kesterson, R. & Wallis, D., 7 Dec 2021, In: Journal of Personalized Medicine. 11, 12, 1320.Research output: Contribution to journal › Article › peer-review
Open Access -
2020
G-quadruplex ligands mediate downregulation of DUX4 expression
Ciszewski, L., Lu-Nguyen, N., Slater, A., Brennan, A., Williams, H. E. L., Dickson, G., Searle, M. S. & Popplewell, L., 17 Mar 2020, In: Nucleic Acids Research. 48, 8, p. 4179-4194 16 p., gkaa146.Research output: Contribution to journal › Article › peer-review
Open Access -
2018
Antisense Oligonucleotide Targeting of 3'-UTR of mRNA for Expression Knockdown
Golshirazi, G., Ciszewski, L., Lu-Nguyen, N. & Popplewell, L., 1 Sept 2018, (E-pub ahead of print) In: Methods in Molecular Biology. 1828, p. 91-124 34 p.Research output: Contribution to journal › Article › peer-review
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2016
Antisense targeting of 3′ end elements involved in DUX4 mRNA processing is an efficient therapeutic strategy for facioscapulohumeral dystrophy: a new gene-silencing approach
Marsollier, A-C., Ciszewski, L., Mariot, V., Popplewell, L., Voit, T., Dickson, G. & Dumonceaux, J., 15 Apr 2016, In: Human Molecular Genetics. 25, 8, p. 1468-1478 11 p.Research output: Contribution to journal › Article › peer-review
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