Antisense targeting of 3′ end elements involved in DUX4 mRNA processing is an efficient therapeutic strategy for facioscapulohumeral dystrophy: a new gene-silencing approach

Anne-Charlotte Marsollier, Lukasz Ciszewski, Virginie Mariot, Linda Popplewell, Thomas Voit, George Dickson, Julie Dumonceaux

Research output: Contribution to journalArticlepeer-review

36 Downloads (Pure)
Original languageEnglish
Pages (from-to)1468-1478
Number of pages11
JournalHuman Molecular Genetics
Issue number8
Early online date19 Jan 2016
Publication statusPublished - 15 Apr 2016

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