Generation of a de novo intronic junction in the DMD gene through CRISPR/Cas genome editing as a potential therapy for a high proportion of Duchenne muscular dystrophy patients.

Monica Rebeca Gil Garzon

Research output: ThesisDoctoral Thesis

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Original languageEnglish
Awarding Institution
  • Royal Holloway, University of London
  • Popplewell, Linda, Supervisor
  • Malerba, Alberto, Supervisor
Award date1 Jan 2024
Publication statusUnpublished - 2023

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