Delivery of AAV2/9-microdystrophin genes incorporating helix 1 of the coiled-coil motif in the C-terminal domain of dystrophin improves muscle pathology and restores the level of α1-syntrophin and α-dystrobrevin in skeletal muscles of mdx mice

Taeyoung Koo, Alberto Malerba, Takis Athanasopoulos, Capucine Trollet, Luisa Boldrin, Arnaud Ferry, Linda J Popplewell, Helen Foster, Keith Foster, George Dickson

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
JournalHuman Gene Therapy
Publication statusPublished - 2011

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