Phase I study of dystrophin plasmid-based gene therapy in Duchenne/Becker muscular dystrophy

Norma B Romero, Serge Braun, Olivier Benveniste, France Leturcq, Jean-Yves Hogrel, Glenn E Morris, Annie Barois, Bruno Eymard, Christine Payan, Véronique Ortega, Anne-Laure Boch, Lise Lejean, Christine Thioudellet, Brigitte Mourot, Christophe Escot, Aurore Choquel, Dominique Recan, Jean-Claude Kaplan, George Dickson, David KlatzmannValérie Molinier-Frenckel, Jean-Gérard Guillet, Patrick Squiban, Serge Herson, Michel Fardeau

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)1065-76
Number of pages12
JournalHuman Gene Therapy
Issue number11
Publication statusPublished - 2004


  • Adolescent
  • Adult
  • Biopsy
  • Cohort Studies
  • Dystrophin
  • Gene Therapy
  • Gene Transfer Techniques
  • Genetic Vectors
  • Histocompatibility Testing
  • Humans
  • Immunohistochemistry
  • Middle Aged
  • Models, Genetic
  • Muscle, Skeletal
  • Muscles
  • Muscular Dystrophy, Duchenne
  • Plasmids
  • Promoter Regions, Genetic
  • RNA, Messenger
  • Reverse Transcriptase Polymerase Chain Reaction
  • Time Factors

Cite this