Optimized lentiviral vector to restore full-length dystrophin via a cell-mediated approach in a mouse model of Duchenne muscular dystrophy

Jinhong Meng, Marc Moore, John Counsell, Francesco Muntoni, Linda Popplewell, Jennifer Morgan

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)491-507
Number of pages17
JournalMolecular Therapy - Methods and Clinical Development
Early online date1 May 2022
Publication statusPublished - 9 Jun 2022

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