Long-Term Systemic Treatment of a Mouse Model Displaying Chronic FSHD-like Pathology with Antisense Therapeutics That Inhibit DUX4 Expression

Ngoc Lu-Nguyen, George Dickson, Alberto Malerba, Linda Popplewell

Research output: Contribution to journal › Article › peer-review

77 Downloads (Pure)

1 results

Finished

Development of cell-penetrating peptide-conjugated antisense oligonucleotides for the treatment of Fascioscapulohumeral Muscular Dystrophy
Lu-Nguyen, N. (Researcher), Dickson, G. (CoPI) & Popplewell, L. (PI)
Muscular Dystrophy UK
1/10/16 → 31/10/18
Project: Research