Adeno-associated virus vector gene transfer and sarcolemmal expression of a 144 kDa micro-dystrophin effectively restores the dystrophin-associated protein complex and inhibits myofibre degeneration in nude/mdx mice

Stewart A Fabb, Dominic J Wells, Patricia Serpente, George Dickson

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)733-41
Number of pages9
JournalHuman Molecular Genetics
Volume11
Issue number7
Publication statusPublished - 2002

Keywords

  • Animals
  • Cell Nucleus
  • Dependovirus
  • Dystrophin
  • Gene Therapy
  • Gene Transfer Techniques
  • Genetic Vectors
  • Immunohistochemistry
  • Mice
  • Mice, Inbred mdx
  • Mice, Nude
  • Muscle Fibers, Skeletal
  • Muscular Dystrophy, Duchenne
  • Sarcolemma

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