Translating the genomics revolution : the need for an international gene therapy consortium for monogenic diseases. / Tremblay, Jacques P; Xiao, Xiao; Aartsma-Rus, Annemieke; Barbas, Carlos; Blau, Helen M; Bogdanove, Adam J; Boycott, Kym; Braun, Serge; Breakefield, Xandra O; Bueren, Juan A; Buschmann, Michael; Byrne, Barry J; Calos, Michele; Cathomen, Toni; Chamberlain, Jeffrey; Chuah, Marinee; Cornetta, Kenneth; Davies, Kay E; Dickson, J George; Duchateau, Philippe; Flotte, Terence R; Gaudet, Daniel; Gersbach, Charles A; Gilbert, Renald; Glorioso, Joseph; Herzog, Roland W; High, Katherine A; Huang, Wenlin; Huard, Johnny; Joung, J Keith; Liu, Depei; Liu, Dexi; Lochmüller, Hanns; Lustig, Lawrence; Martens, Jeffrey; Massie, Bernard; Mavilio, Fulvio; Mendell, Jerry R; Nathwani, Amit; Ponder, Katherine; Porteus, Matthew; Puymirat, Jack; Samulski, Jude; Takeda, Shin'ichi; Thrasher, Adrian; VandenDriessche, Thierry; Wei, Yuquan; Wilson, James M; Wilton, Steve D; Wolfe, John H; Gao, Guangping.
In: Molecular Therapy, Vol. 21, No. 2, 02.2013, p. 266-8.Research output: Contribution to journal › Article
Original language | English |
---|---|
Pages (from-to) | 266-8 |
Number of pages | 3 |
Journal | Molecular Therapy |
Volume | 21 |
Issue number | 2 |
DOIs | |
Publication status | Published - Feb 2013 |
ID: 19254365