Systemic Antisense Therapeutics for Dystrophin and Myostatin Exon Splice Modulation Improve Muscle Pathology of Adult mdx Mice. / Lu-Nguyen, Ngoc; Malerba, Alberto; Popplewell, Linda; Schnell, Fred; Hanson, Gunnar; Dickson, George.
In: Molecular therapy. Nucleic acids, Vol. 6, 17.03.2017, p. 15-28.Research output: Contribution to journal › Article
Original language | English |
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Pages (from-to) | 15-28 |
Number of pages | 14 |
Journal | Molecular therapy. Nucleic acids |
Volume | 6 |
Early online date | 14 Dec 2016 |
DOIs | |
Publication status | Published - 17 Mar 2017 |
Activity: Talk or presentation › Oral presentation
Activity: Talk or presentation › Oral presentation
Activity: Talk or presentation › Oral presentation
ID: 27903772