Systematic review and meta-analysis determining the benefits of in vivo genetic therapy in spinal muscular atrophy rodent models

Ellie Chilcott, Evalyne Muiruri, Theodore C. Hirst, R. J. Yáñez-Muñoz

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
JournalGene Therapy
DOIs
Publication statusPublished - 6 Oct 2021

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