Reversible immortalisation enables genetic correction of human muscle progenitors and engineering of next-generation human artificial chromosomes for Duchenne muscular dystrophy

Sara Benedetti, Narumi Uno, Hidetoshi Hoshiya, Martina Ragazzi, Giulia Ferrari, Yasuhiro Kazuki, Louise Anne Moyle, Rossana Tonlorenzi, Angelo Lombardo, Soraya Chaouch, Vincent Mouly, Marc Moore, Linda Popplewell, Kanako Kazuki, Motonobu Katoh, Luigi Naldini, George Dickson, Graziella Messina, Mitsuo Oshimura, Giulio CossuFrancesco Saverio Tedesco

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)254-275
Number of pages22
JournalEMBO Reports
Volume10
Issue number2
Early online date14 Dec 2017
DOIs
Publication statusPublished - 1 Feb 2018

Keywords

  • Journal Article

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