piggyBac transposons expressing full-length human dystrophin enable genetic correction of dystrophic mesoangioblasts

Mariana Loperfido, Susan Jarmin, Sumitava Dastidar, Mario Di Matteo, Ilaria Perini, Marc Moore, Nisha Nair, Ermira Samara-Kuko, Takis Athanasopoulos, Francesco Saverio Tedesco, George Dickson, Maurilio Sampaolesi, Thierry VandenDriessche, Marinee K Chuah

Research output: Contribution to journalArticlepeer-review

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Original languageEnglish
Pages (from-to)744-760
Number of pages17
JournalNucleic Acids Research
Volume44
Issue number2
Early online date17 Dec 2015
DOIs
Publication statusPublished - 29 Jan 2016

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