Phase I study of dystrophin plasmid-based gene therapy in Duchenne/Becker muscular dystrophy. / Romero, Norma B; Braun, Serge; Benveniste, Olivier; Leturcq, France; Hogrel, Jean-Yves; Morris, Glenn E; Barois, Annie; Eymard, Bruno; Payan, Christine; Ortega, Véronique; Boch, Anne-Laure; Lejean, Lise; Thioudellet, Christine; Mourot, Brigitte; Escot, Christophe; Choquel, Aurore; Recan, Dominique; Kaplan, Jean-Claude; Dickson, George; Klatzmann, David; Molinier-Frenckel, Valérie; Guillet, Jean-Gérard; Squiban, Patrick; Herson, Serge; Fardeau, Michel.
In: Human Gene Therapy, Vol. 15, No. 11, 2004, p. 1065-76.Research output: Contribution to journal › Article › peer-review
Original language | English |
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Pages (from-to) | 1065-76 |
Number of pages | 12 |
Journal | Human Gene Therapy |
Volume | 15 |
Issue number | 11 |
DOIs | |
Publication status | Published - 2004 |
ID: 958146