PABPN1 gene therapy for oculopharyngeal muscular dystrophy

A Malerba, P Klein, Houria Bachtarzi, S A Jarmin, G Cordova, A Ferry, V Strings, M Polay Espinoza, K Mamchaoui, S C Blumen, J Lacau St Guily, V Mouly, M Graham, G Butler-Browne, D A Suhy, C Trollet, George Dickson

Research output: Contribution to journalArticlepeer-review

105 Downloads (Pure)
Original languageEnglish
Article number14848
Pages (from-to)1-14
Number of pages14
JournalNature Communications
Volume8
DOIs
Publication statusPublished - 31 Mar 2017

Keywords

  • Journal Article

Cite this