PABPN1 gene therapy for oculopharyngeal muscular dystrophy. / Malerba, A; Klein, P; Bachtarzi, Houria; Jarmin, S A; Cordova, G; Ferry, A; Strings, V; Espinoza, M Polay; Mamchaoui, K; Blumen, S C; St Guily, J Lacau; Mouly, V; Graham, M; Butler-Browne, G; Suhy, D A; Trollet, C; Dickson, George.

In: Nature Communications, Vol. 8, 14848, 31.03.2017, p. 1-14.

Research output: Contribution to journalArticlepeer-review



Original languageEnglish
Article number14848
Pages (from-to)1-14
Number of pages14
JournalNature Communications
Publication statusPublished - 31 Mar 2017
This open access research output is licenced under a Creative Commons Attribution-NonCommercial-NoDerivs 3.0 Unported License.

ID: 27931874