Muscle overexpression of Klf15 via an AAV8-Spc5-12 construct does not provide benefits in spinal muscular atrophy mice

Nina Ahlskog, Daniel Hayler-Pountney, Anja Krueger, Sabrina Kubinski, Peter Claus, Suzan M. Hammond, Matthew J.A. Wood, Rafael J. Yáñez-Muñoz, Melissa Bowerman

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)1-11
Number of pages11
JournalGene Therapy
DOIs
Publication statusPublished - 20 Apr 2020

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