Long-Term Systemic Administration of Unconjugated Morpholino Oligomers for Therapeutic Expression of Dystrophin by Exon Skipping in Skeletal Muscle: Implications for Cardiac Muscle Integrity

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)293-298
Number of pages6
JournalNucleic Acid Therapeutics
Volume21
Issue number4
DOIs
Publication statusPublished - Aug 2011

Keywords

  • DUCHENNE MUSCULAR-DYSTROPHY
  • LINKED DILATED CARDIOMYOPATHY
  • MDX MICE
  • DEFICIENT MICE
  • GENE
  • DELIVERY
  • MOUSE
  • RESTORATION
  • DYSFUNCTION
  • RESCUE

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