Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-escalation, proof-of-concept study. / Kinali, Maria; Arechavala-Gomeza, Virginia; Feng, Lucy; Cirak, Sebahattin; Hunt, David; Adkin, Carl; Guglieri, Michela; Ashton, Emma; Abbs, Stephen; Nihoyannopoulos, Petros; Garralda, Maria Elena; Rutherford, Mary; McCulley, Caroline; Popplewell, Linda; Graham, Ian R; Dickson, George; Wood, Matthew J A; Wells, Dominic J; Wilton, Steve D; Kole, Ryszard; Straub, Volker; Bushby, Kate; Sewry, Caroline; Morgan, Jennifer E; Muntoni, Francesco.
In: Lancet Neurology, Vol. 8, No. 10, 10.2009, p. 918-928.Research output: Contribution to journal › Article
Published
| Original language | English |
|---|---|
| Pages (from-to) | 918-928 |
| Number of pages | 11 |
| Journal | Lancet Neurology |
| Volume | 8 |
| Issue number | 10 |
| Early online date | 26 Aug 2009 |
| DOIs | |
| State | Published - Oct 2009 |
This open access research output is licenced under a Creative Commons Attribution-NonCommercial-NoDerivs 3.0 Unported License.
ID: 961812