Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-escalation, proof-of-concept study. / Kinali, Maria; Arechavala-Gomeza, Virginia; Feng, Lucy; Cirak, Sebahattin; Hunt, David; Adkin, Carl; Guglieri, Michela; Ashton, Emma; Abbs, Stephen; Nihoyannopoulos, Petros; Garralda, Maria Elena; Rutherford, Mary; McCulley, Caroline; Popplewell, Linda; Graham, Ian R; Dickson, George; Wood, Matthew J A; Wells, Dominic J; Wilton, Steve D; Kole, Ryszard; Straub, Volker; Bushby, Kate; Sewry, Caroline; Morgan, Jennifer E; Muntoni, Francesco.

In: Lancet Neurology, Vol. 8, No. 10, 10.2009, p. 918-928.

Research output: Contribution to journalArticlepeer-review

  • Maria Kinali
  • Virginia Arechavala-Gomeza
  • Lucy Feng
  • Sebahattin Cirak
  • David Hunt
  • Carl Adkin
  • Michela Guglieri
  • Emma Ashton
  • Stephen Abbs
  • Petros Nihoyannopoulos
  • Maria Elena Garralda
  • Mary Rutherford
  • Caroline McCulley
  • Ian R Graham
  • Matthew J A Wood
  • Dominic J Wells
  • Steve D Wilton
  • Ryszard Kole
  • Volker Straub
  • Kate Bushby
  • Caroline Sewry
  • Jennifer E Morgan
  • Francesco Muntoni
Original languageEnglish
Pages (from-to)918-928
Number of pages11
JournalLancet Neurology
Issue number10
Early online date26 Aug 2009
Publication statusPublished - Oct 2009
This open access research output is licenced under a Creative Commons Attribution-NonCommercial-NoDerivs 3.0 Unported License.

ID: 961812