Functional Rescue of Dystrophin Deficiency in Mice Caused by Frameshift Mutations Using Campylobacter jejuni Cas9

Taeyoung Koo, Ngoc B Lu-Nguyen, Alberto Malerba, Eunji Kim, Daesik Kim, Ornella Cappellari, Hee-Yeon Cho, George Dickson, Linda Popplewell, Jin-Soo Kim

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)1529-1538
Number of pages10
JournalMolecular Therapy
Volume26
Issue number6
Early online date30 Mar 2018
DOIs
Publication statusPublished - 6 Jun 2018

Keywords

  • Journal Article

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