Dose-dependent microdystrophin expression enhancement in cardiac muscle by a cardiac specific regulatory element

Alberto Malerba, Chiara Sidoli, Ngoc B Lu-Nguyen, Shanthi Herath, Anita Le Heron, Hayder Abdul-Razak, Susan Jarmin, Thierry Vandendriessche, Marinee K L Chuah, George Dickson, Linda J Popplewell

Research output: Contribution to journalArticlepeer-review

45 Downloads (Pure)
Original languageEnglish
JournalHuman Gene Therapy
Early online date26 Mar 2021
DOIs
Publication statusE-pub ahead of print - 26 Mar 2021

Cite this