Delivery of AAV2/9-microdystrophin genes incorporating helix 1 of the coiled-coil motif in the C-terminal domain of dystrophin improves muscle pathology and restores the level of α1-syntrophin and α-dystrobrevin in skeletal muscles of mdx mice. / Koo, Taeyoung; Malerba, Alberto; Athanasopoulos, Takis; Trollet, Capucine; Boldrin, Luisa; Ferry, Arnaud; Popplewell, Linda J; Foster, Helen; Foster, Keith; Dickson, George.
In: Human Gene Therapy, 2011.Research output: Contribution to journal › Article › peer-review
Original language | English |
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Journal | Human Gene Therapy |
DOIs | |
Publication status | Published - 2011 |
ID: 1448674