Current Progress in Therapeutic Gene Editing for Monogenic Diseases

Versha Prakash, Marc Moore, Rafael J Yáñez-Muñoz

Research output: Contribution to journalReview articlepeer-review

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Original languageEnglish
Pages (from-to)465-474
Number of pages10
JournalMolecular Therapy
Volume24
Issue number3
DOIs
Publication statusPublished - Mar 2016

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