Cell engineering for muscle gene therapy: Extemporaneous production of retroviral vector packaging macrophages using defective herpes simplex virus type 1 vectors harbouring gag, pol, env genes

E Parrish, E Peltekian, G Dickson, A L Epstein, L Garcia

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)173-180
Number of pages8
JournalCYTOTECHNOLOGY
Volume30
Issue number1-3
Publication statusPublished - 1999

Keywords

  • gene therapy
  • HSV1-amplicon
  • macrophages
  • muscle dystrophy
  • retrovirus packaging
  • ADENOVIRUS-MEDIATED TRANSFER
  • MONOCYTE-DERIVED MACROPHAGES
  • SKELETAL-MUSCLE
  • IN-VIVO
  • MINIDYSTROPHIN GENE
  • MDX MICE
  • EXPRESSION
  • EFFICIENT
  • MOUSE
  • TRANSDUCTION

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