Antisense-induced Myostatin Exon Skipping Leads to Muscle Hypertrophy in Mice Following Octa-guanidine Morpholino Oligomer Treatment

Jagjeet K. Kang, Alberto Malerba, Linda Popplewell, Keith Foster, George Dickson

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)159-164
Number of pages6
JournalMolecular Therapy
Volume19
Issue number1
DOIs
Publication statusPublished - Jan 2011

Keywords

  • RESTORES DYSTROPHIN EXPRESSION
  • SKELETAL-MUSCLE
  • MUSCULAR-DYSTROPHY
  • SPLICING ENHANCERS
  • MDX MICE
  • MESSENGER-RNA
  • ADULT MICE
  • GENE
  • OLIGONUCLEOTIDES
  • PATHOLOGY

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