Adeno-Associated Virus (AAV) Mediated Dystrophin Gene Transfer Studies and Exon Skipping Strategies for Duchenne Muscular Dystrophy (DMD). / Kawecka, Klaudia; Theodoulides, Michael; Hasoglu, Yalin; Jarmin, Susan; Kymalainen, Hanna; Le-Heron, Anita; Popplewell, Linda; Malerba, Alberto; Dickson, George; Athanasopoulos, Takis.
In: Current Gene Therapy, Vol. 15, No. 4, 2015, p. 395-415.Research output: Contribution to journal › Article › peer-review
Original language | English |
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Pages (from-to) | 395-415 |
Number of pages | 21 |
Journal | Current Gene Therapy |
Volume | 15 |
Issue number | 4 |
Early online date | 1 Aug 2015 |
DOIs | |
Publication status | Published - 2015 |
ID: 25339205