Project relations

• Combination Antisense Treatment for Duchenne Muscular Dystrophy: Open Reading Frame Rescue of Dystrophin in conjunction with Destructive Exon Skipping of Myostatin mRNA

  Project: Research

Prizes

• Travel Grant - Oligonucleotide Therapeutics Society (USA)

  Prize: Prize (including medals and awards)

• Fellowship - European Cooperation in Science and Technology

  Prize: Prize (including medals and awards)

• Fellowship - European Cooperation in Science and Technology

  Prize: Prize (including medals and awards)

• Travel Grant - British Society for Gene and Cell Therapy

  Prize: Prize (including medals and awards)

Activities

• Networking towards clinical application of antisense-mediated exon skipping (Portugal)

  Activity: Participating in or organising an event › Participation in conference

• Workshop on delivery and delivery to the central nervous system (Spain)

  Activity: Talk or presentation › Oral presentation

• Hellenic Society of Gene Therapy and Regenerative Medicine Congress (Greece)

  Activity: Talk or presentation › Oral presentation

• 10th Annual Meeting of The Oligonucleotide Therapeutics Society (USA)

  Activity: Talk or presentation › Oral presentation

• MDEX Consortium Meeting (UK)

  Activity: Participating in or organising an event › Participation in workshop, seminar, course

• 11th Annual Meeting of The Oligonucleotide Therapeutics Society (Netherlands)

  Activity: Participating in or organising an event › Participation in conference

Research outputs

• Systemic Intravenous Administration of Antisense Therapeutics for Combinatorial Dystrophin and Myostatin Exon Splice Modulation

  Research output: Contribution to journal › Article

• Systemic Antisense Therapeutics for Dystrophin and Myostatin Exon Splice Modulation Improve Muscle Pathology of Adult mdx Mice

  Research output: Contribution to journal › Article

• Functional muscle recovery following dystrophin and myostatin exon splice modulation in aged mdx mice

  Research output: Contribution to journal › Article

• Myostatin inhibition in combination with antisense oligonucleotide therapy improves outcomes in spinal muscular atrophy

  Research output: Contribution to journal › Article

• Targeting TGFβ Signaling to Address Fibrosis Using Antisense Oligonucleotides

  Research output: Contribution to journal › Review article