1. 2015
  2. Published

    Decay in survival motor neuron and plastin 3 levels during differentiation of iPSC-derived human motor neurons

    Boza-Morán, M. G., Martínez-Hernández, R., Bernal, S., Wanisch, K., Also-Rallo, E., le Heron, A., Alías, L., Denis, C., Girard, M., Yee, J-K., Tizzano, E. F. & Yanez, R. 26 Jun 2015 In : Scientific reports. 5, 17 p., 11696

    Research output: Contribution to journalArticle

  3. Published

    Progress on gene therapy, cell therapy and pharmacological strategies towards the treatment of Oculopharyngeal Muscular Dystrophy

    Harish, P., Malerba, A., Dickson, G. & Bachtarzi, H. 19 May 2015 In : Human Gene Therapy. 26, 5, p. 286-292 7 p.

    Research output: Contribution to journalArticle

  4. Published
  5. Published

    Enhanced efficacy of the CDNF/MANF family by combined intranigral overexpression in the 6-OHDA rat model of Parkinson's disease

    Cordero-Llana, Ó., Houghton, B. C., Rinaldi, F., Taylor, H., Yáñez-Muñoz, R. J., Uney, J. B., Wong, L-F. & Caldwell, M. A. Feb 2015 In : Molecular Therapy. 23, 2, p. 244-54 11 p.

    Research output: Contribution to journalArticle

  6. Published

    Annotation and functional assignment of the genes for the C-30 carotenoid pathways from the genomes of two bacteria: Bacillus indicus and Bacillus firmus

    Steiger, S., Perez-Fons, L., Cutting, S. M., Fraser, P. D. & Sandmann, G. 1 Jan 2015 In : Microbiology (Reading, England). 161, 1, p. 194-202 9 p.

    Research output: Contribution to journalArticle

  7. Published

    Abnormal splicing switch of DMD's penultimate exon compromises muscle fibre maintenance in myotonic dystrophy

    Athanasopoulos, T. , Dickson, G. & 19 others Rau, F., Lainé, J., Ramanoudjame, L., Ferry, A., Arandel, L., Delalande, O., Jollet, A., Dingli, F., Lee, K-Y., Peccate, C., Lorain, S., Kabashi, E., Koo, T., Loew, D., Swanson, M. S., Le Rumeur, E., Allamand, V., Marie, J. & Furling, D. 2015 In : Nature Communications. 6, 7205

    Research output: Contribution to journalArticle

  8. Published

    Adeno-Associated Virus (AAV) Mediated Dystrophin Gene Transfer Studies and Exon Skipping Strategies for Duchenne Muscular Dystrophy (DMD)

    Kawecka, K., Theodoulides, M., Hasoglu, Y., Jarmin, S., Kymalainen, H., Le-Heron, A., Popplewell, L., Malerba, A., Dickson, G. & Athanasopoulos, T. 2015 In : Current Gene Therapy. 15, 4, p. 395-415 21 p.

    Research output: Contribution to journalArticle

  9. Published
  10. Published

    Mitochondrial dysfunction reveals the role of mRNA poly(a) tail regulation in oculopharyngeal muscular dystrophy pathogenesis

    Chartier, A., Klein, P., Pierson, S., Barbezier, N., Gidaro, T., Casas, F., Carberry, S., Dowling, P., Maynadier, L., Bellec, M., Oloko, M., Jardel, C., Moritz, B., Dickson, G., Mouly, V., Ohlendieck, K., Butler-Browne, G., Trollet, C. & Simonelig, M. 2015 In : PLoS genetics. 11, 3, p. e1005092

    Research output: Contribution to journalArticle

  11. Published

    New experimental therapies for status epilepticus in pre-clinical development

    Walker, M. & Williams, R. 2015 In : Epilepsy and Behaviour.

    Research output: Contribution to journalScientific review

  12. Forthcoming

    Valproic acid protects against haemorrhagic shock-induced signalling changes via PPARγ activation in an in vitro model

    Zuckermann, A., LaRagione, R., Baines, D. & Williams, R. 2015 In : British Journal of Pharmacology.

    Research output: Contribution to journalArticle

  13. 2014
  14. Published

    Synthesis of hybrid anticancer agents based on kinase and histone deacetylase inhibitors

    Patel, H., Chuckowree, I., Coxhead, P., Guille, M., Wang, M., Zuckermann, A., Williams, R., Librizzi, M., Paranal, R. M., Bradner, J. E. & Spencer, J. 1 Dec 2014 In : MedChemComm. 12, p. 1829-1833 5 p.

    Research output: Contribution to journalArticle

  15. Published

    Primary Chemical Sequence Ultimately Determines Crystal Thickness in Segmented All-Aliphatic Copolymers

    Odarchenko, Y. I., Anokhin, D. V., Doblas, D., Rosenthal, M., Hernandez, J. J., Vidal, L., Sijbrandi, N. J., Kimenai, A. J., Mes, E. P. C., Broos, R., Bar, G., Dijkstra, P. J., Feijen, J., Soloviev, M. & Ivanov, D. A. 25 Nov 2014 In : Macromolecules. 47, 22, p. 7890-7899 10 p.

    Research output: Contribution to journalArticle

  16. Published

    Genetic interactions between planar cell polarity genes cause diverse neural tube defects in mice

    Murdoch, J. N., Damrau, C., Paudyal, A., Bogani, D., Wells, S., Greene, N. D. E., Stanier, P. & Copp, A. J. Oct 2014 In : Disease Models and Mechanisms. 7, 10, p. 1153-63 11 p.

    Research output: Contribution to journalArticle

  17. Published

    Genome-Wide Computational Analysis Reveals Cardiomyocyte-Specific Transcriptional CIS-Regulatory Motifs that Enable Efficient Cardiac Gene Therapy

    Rincon, M. Y., Sarcar, S., Danso-Abeam, D., Keyaerts, M., Matrai, J., Samara-Kuko, E., Acosta-Sanchez, A., Athanasopoulos, T., Dickson, G., Lahoutte, T., De Bleser, P., VandenDriessche, T. & Chuah, M. K. 8 Sep 2014 In : Molecular Therapy.

    Research output: Contribution to journalArticle

  18. Published

    Local Overexpression of the Myostatin Propeptide Increases Glucose Transporter Expression and Enhances Skeletal Muscle Glucose Disposal

    Cleasby, M. E., Jarmin, S., Eilers, W., Elashry, M., Andersen, D. K., Dickson, G. & Foster, K. 1 Apr 2014 In : American Journal of Physiology. Endocrinology and Metabolism.

    Research output: Contribution to journalArticle

  19. Published

    Transgenic expression of human glial cell line-derived neurotrophic factor (hGDNF) from integration-deficient lentiviral vectors is neuroprotective in a rodent model of Parkinson's disease

    Lu-Nguyen, N. B., Broadstock, M., Schliesser, M. G., Bartholomae, C., von Kalle, C., Schmidt, M. & Yáñez-Muñoz, R. J. 18 Mar 2014 In : Human Gene Therapy.

    Research output: Contribution to journalArticle

  20. Published

    Long-term episomal transgene expression from mitotically stable integration-deficient lentiviral vectors (IDLVs)

    Kymalainen, H., Appelt, J-U., Giordano, F. A., Davies, A. F., Ogilvie, C. M., Ahmed, S. G., Laufs, S., Schmidt, M., Bode, J., Yáñez-Muñoz, R. J. & Dickson, G. 2 Feb 2014 In : Human Gene Therapy.

    Research output: Contribution to journalArticle

  21. Published

    New developments in the use of gene therapy to treat Duchenne muscular dystrophy

    Jarmin, S., Kymalainen, H., Popplewell, L. & Dickson, G. Feb 2014 In : Expert Opinion on Biological Therapy. 14, 2, p. 209-30 22 p.

    Research output: Contribution to journalArticle

  22. Published

    Seizure-induced reduction in PIP3 levels contributes to seizure-activity and is rescued by valproic acid

    Chang, P., Walker, M. C. & Williams, R. Feb 2014 In : Neurobiology of Disease. 62, p. 296–306 10 p.

    Research output: Contribution to journalArticle

  23. Published
  24. Published

    A southern blot protocol to detect chimeric nuclease-mediated gene repair

    Rocca, C. J., Abdul-Razak, H. H., Holmes, M. C., Gregory, P. D. & Yáñez-Muñoz, R. J. 2014 In : Methods in Molecular Biology. 1114, p. 325-38 14 p.

    Research output: Contribution to journalArticle

  25. Published
  26. Published
  27. Published

    Fusion of Ubiquitin to HIV Gag Impairs Human Monocyte-Derived Dendritic Cell Maturation and Reduces Ability to Induce Gag T Cell Responses

    Herath, S., Benlahrech, A., Papagatsias, T., Athanasopoulos, T., Bouzeboudjen, Z., Hervouet, C., Klavinskis, L., Meiser, A., Kelleher, P., Dickson, G. & Patterson, S. 2014 In : PLoS One. 9, 2, p. e88327

    Research output: Contribution to journalArticle

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