1. 2015
  2. Published

    Decay in survival motor neuron and plastin 3 levels during differentiation of iPSC-derived human motor neurons

    Boza-Morán, M. G., Martínez-Hernández, R., Bernal, S., Wanisch, K., Also-Rallo, E., le Heron, A., Alías, L., Denis, C., Girard, M., Yee, J-K., Tizzano, E. F. & Yanez, R. 26 Jun 2015 In : Scientific reports. 5, 17 p., 11696

    Research output: Contribution to journalArticle

  3. Published

    Progress on gene therapy, cell therapy and pharmacological strategies towards the treatment of Oculopharyngeal Muscular Dystrophy

    Harish, P., Malerba, A., Dickson, G. & Bachtarzi, H. 19 May 2015 In : Human Gene Therapy. 26, 5, p. 286-292 7 p.

    Research output: Contribution to journalArticle

  4. Published
  5. Published

    Enhanced efficacy of the CDNF/MANF family by combined intranigral overexpression in the 6-OHDA rat model of Parkinson's disease

    Cordero-Llana, Ó., Houghton, B. C., Rinaldi, F., Taylor, H., Yáñez-Muñoz, R. J., Uney, J. B., Wong, L-F. & Caldwell, M. A. Feb 2015 In : Molecular Therapy. 23, 2, p. 244-54 11 p.

    Research output: Contribution to journalArticle

  6. Published

    Annotation and functional assignment of the genes for the C-30 carotenoid pathways from the genomes of two bacteria: Bacillus indicus and Bacillus firmus

    Steiger, S., Perez-Fons, L., Cutting, S. M., Fraser, P. D. & Sandmann, G. 1 Jan 2015 In : Microbiology (Reading, England). 161, 1, p. 194-202 9 p.

    Research output: Contribution to journalArticle

  7. Published

    Abnormal splicing switch of DMD's penultimate exon compromises muscle fibre maintenance in myotonic dystrophy

    Athanasopoulos, T. , Dickson, G. & 19 others Rau, F., Lainé, J., Ramanoudjame, L., Ferry, A., Arandel, L., Delalande, O., Jollet, A., Dingli, F., Lee, K-Y., Peccate, C., Lorain, S., Kabashi, E., Koo, T., Loew, D., Swanson, M. S., Le Rumeur, E., Allamand, V., Marie, J. & Furling, D. 2015 In : Nature Communications. 6, 7205

    Research output: Contribution to journalArticle

  8. Published

    Adeno-Associated Virus (AAV) Mediated Dystrophin Gene Transfer Studies and Exon Skipping Strategies for Duchenne Muscular Dystrophy (DMD)

    Kawecka, K., Theodoulides, M., Hasoglu, Y., Jarmin, S., Kymalainen, H., Le-Heron, A., Popplewell, L., Malerba, A., Dickson, G. & Athanasopoulos, T. 2015 In : Current Gene Therapy. 15, 4, p. 395-415 21 p.

    Research output: Contribution to journalArticle

  9. Published
  10. Published

    Mitochondrial dysfunction reveals the role of mRNA poly(a) tail regulation in oculopharyngeal muscular dystrophy pathogenesis

    Chartier, A., Klein, P., Pierson, S., Barbezier, N., Gidaro, T., Casas, F., Carberry, S., Dowling, P., Maynadier, L., Bellec, M., Oloko, M., Jardel, C., Moritz, B., Dickson, G., Mouly, V., Ohlendieck, K., Butler-Browne, G., Trollet, C. & Simonelig, M. 2015 In : PLoS genetics. 11, 3, p. e1005092

    Research output: Contribution to journalArticle

  11. Published

    New experimental therapies for status epilepticus in pre-clinical development

    Walker, M. & Williams, R. 2015 In : Epilepsy and Behaviour.

    Research output: Contribution to journalScientific review

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