Translating the genomics revolution: the need for an international gene therapy consortium for monogenic diseases

Jacques P Tremblay; Xiao Xiao; Annemieke Aartsma-Rus; Carlos Barbas; Helen M Blau; Adam J Bogdanove; Kym Boycott; Serge Braun; Xandra O Breakefield; Juan A Bueren; Michael Buschmann; Barry J Byrne; Michele Calos; Toni Cathomen; Jeffrey Chamberlain; Marinee Chuah; Kenneth Cornetta; Kay E Davies; J George Dickson; Philippe Duchateau; Terence R Flotte; Daniel Gaudet; Charles A Gersbach; Renald Gilbert; Joseph Glorioso; Roland W Herzog; Katherine A High; Wenlin Huang; Johnny Huard; J Keith Joung; Depei Liu; Dexi Liu; Hanns Lochmüller; Lawrence Lustig; Jeffrey Martens; Bernard Massie; Fulvio Mavilio; Jerry R Mendell; Amit Nathwani; Katherine Ponder; Matthew Porteus; Jack Puymirat; Jude Samulski; Shin'ichi Takeda; Adrian Thrasher; Thierry VandenDriessche; Yuquan Wei; James M Wilson; Steve D Wilton; John H Wolfe; Guangping Gao

doi:10.1038/mt.2013.4

Translating the genomics revolution: the need for an international gene therapy consortium for monogenic diseases

Jacques P Tremblay
, Xiao Xiao
, Annemieke Aartsma-Rus
, Carlos Barbas
, Helen M Blau
, Adam J Bogdanove
, Kym Boycott
, Serge Braun
, Xandra O Breakefield
, Juan A Bueren
, Michael Buschmann
, Barry J Byrne
, Michele Calos
, Toni Cathomen
, Jeffrey Chamberlain
, Marinee Chuah
, Kenneth Cornetta
, Kay E Davies
, J George Dickson
, Philippe Duchateau

Terence R Flotte, Daniel Gaudet, Charles A Gersbach, Renald Gilbert, Joseph Glorioso, Roland W Herzog, Katherine A High, Wenlin Huang, Johnny Huard, J Keith Joung, Depei Liu, Dexi Liu, Hanns Lochmüller, Lawrence Lustig, Jeffrey Martens, Bernard Massie, Fulvio Mavilio, Jerry R Mendell, Amit Nathwani, Katherine Ponder, Matthew Porteus, Jack Puymirat, Jude Samulski, Shin'ichi Takeda, Adrian Thrasher, Thierry VandenDriessche, Yuquan Wei, James M Wilson, Steve D Wilton, John H Wolfe, Guangping Gao

Research output: Contribution to journal › Article

Original language	English
Pages (from-to)	266-8
Number of pages	3
Journal	Molecular Therapy
Volume	21
Issue number	2
DOIs	https://doi.org/10.1038/mt.2013.4
Publication status	Published - Feb 2013

Keywords

Biomedical Research
Genetic Therapy
Genomics
Humans
International Cooperation

Access to Document

10.1038/mt.2013.4

Cite this

Tremblay, J. P., Xiao, X., Aartsma-Rus, A., Barbas, C., Blau, H. M., Bogdanove, A. J., Boycott, K., Braun, S., Breakefield, X. O., Bueren, J. A., Buschmann, M., Byrne, B. J., Calos, M., Cathomen, T., Chamberlain, J., Chuah, M., Cornetta, K., Davies, K. E., Dickson, J. G., ... Gao, G. (2013). Translating the genomics revolution: the need for an international gene therapy consortium for monogenic diseases. Molecular Therapy, 21(2), 266-8. https://doi.org/10.1038/mt.2013.4

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title = "Translating the genomics revolution: the need for an international gene therapy consortium for monogenic diseases",

keywords = "Biomedical Research, Genetic Therapy, Genomics, Humans, International Cooperation",

author = "Tremblay, \{Jacques P\} and Xiao Xiao and Annemieke Aartsma-Rus and Carlos Barbas and Blau, \{Helen M\} and Bogdanove, \{Adam J\} and Kym Boycott and Serge Braun and Breakefield, \{Xandra O\} and Bueren, \{Juan A\} and Michael Buschmann and Byrne, \{Barry J\} and Michele Calos and Toni Cathomen and Jeffrey Chamberlain and Marinee Chuah and Kenneth Cornetta and Davies, \{Kay E\} and Dickson, \{J George\} and Philippe Duchateau and Flotte, \{Terence R\} and Daniel Gaudet and Gersbach, \{Charles A\} and Renald Gilbert and Joseph Glorioso and Herzog, \{Roland W\} and High, \{Katherine A\} and Wenlin Huang and Johnny Huard and Joung, \{J Keith\} and Depei Liu and Dexi Liu and Hanns Lochm{\"u}ller and Lawrence Lustig and Jeffrey Martens and Bernard Massie and Fulvio Mavilio and Mendell, \{Jerry R\} and Amit Nathwani and Katherine Ponder and Matthew Porteus and Jack Puymirat and Jude Samulski and Shin'ichi Takeda and Adrian Thrasher and Thierry VandenDriessche and Yuquan Wei and Wilson, \{James M\} and Wilton, \{Steve D\} and Wolfe, \{John H\} and Guangping Gao",

year = "2013",

month = feb,

doi = "10.1038/mt.2013.4",

language = "English",

volume = "21",

pages = "266--8",

journal = "Molecular Therapy",

issn = "1525-0016",

publisher = "Cell Press",

number = "2",

}

Tremblay, JP, Xiao, X, Aartsma-Rus, A, Barbas, C, Blau, HM, Bogdanove, AJ, Boycott, K, Braun, S, Breakefield, XO, Bueren, JA, Buschmann, M, Byrne, BJ, Calos, M, Cathomen, T, Chamberlain, J, Chuah, M, Cornetta, K, Davies, KE, Dickson, JG, Duchateau, P, Flotte, TR, Gaudet, D, Gersbach, CA, Gilbert, R, Glorioso, J, Herzog, RW, High, KA, Huang, W, Huard, J, Joung, JK, Liu, D, Liu, D, Lochmüller, H, Lustig, L, Martens, J, Massie, B, Mavilio, F, Mendell, JR, Nathwani, A, Ponder, K, Porteus, M, Puymirat, J, Samulski, J, Takeda, S, Thrasher, A, VandenDriessche, T, Wei, Y, Wilson, JM, Wilton, SD, Wolfe, JH & Gao, G 2013, 'Translating the genomics revolution: the need for an international gene therapy consortium for monogenic diseases', Molecular Therapy, vol. 21, no. 2, pp. 266-8. https://doi.org/10.1038/mt.2013.4

TY - JOUR

T1 - Translating the genomics revolution

T2 - the need for an international gene therapy consortium for monogenic diseases

AU - Tremblay, Jacques P

AU - Xiao, Xiao

AU - Aartsma-Rus, Annemieke

AU - Barbas, Carlos

AU - Blau, Helen M

AU - Bogdanove, Adam J

AU - Boycott, Kym

AU - Braun, Serge

AU - Breakefield, Xandra O

AU - Bueren, Juan A

AU - Buschmann, Michael

AU - Byrne, Barry J

AU - Calos, Michele

AU - Cathomen, Toni

AU - Chamberlain, Jeffrey

AU - Chuah, Marinee

AU - Cornetta, Kenneth

AU - Davies, Kay E

AU - Dickson, J George

AU - Duchateau, Philippe

AU - Flotte, Terence R

AU - Gaudet, Daniel

AU - Gersbach, Charles A

AU - Gilbert, Renald

AU - Glorioso, Joseph

AU - Herzog, Roland W

AU - High, Katherine A

AU - Huang, Wenlin

AU - Huard, Johnny

AU - Joung, J Keith

AU - Liu, Depei

AU - Liu, Dexi

AU - Lochmüller, Hanns

AU - Lustig, Lawrence

AU - Martens, Jeffrey

AU - Massie, Bernard

AU - Mavilio, Fulvio

AU - Mendell, Jerry R

AU - Nathwani, Amit

AU - Ponder, Katherine

AU - Porteus, Matthew

AU - Puymirat, Jack

AU - Samulski, Jude

AU - Takeda, Shin'ichi

AU - Thrasher, Adrian

AU - VandenDriessche, Thierry

AU - Wei, Yuquan

AU - Wilson, James M

AU - Wilton, Steve D

AU - Wolfe, John H

AU - Gao, Guangping

PY - 2013/2

Y1 - 2013/2

KW - Biomedical Research

KW - Genetic Therapy

KW - Genomics

KW - Humans

KW - International Cooperation

U2 - 10.1038/mt.2013.4

DO - 10.1038/mt.2013.4

M3 - Article

C2 - 23369965

SN - 1525-0016

VL - 21

SP - 266

EP - 268

JO - Molecular Therapy

JF - Molecular Therapy

IS - 2

ER -