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The administration of antisense oligonucleotide golodirsen reduces pathological regeneration in patients with Duchenne muscular dystrophy

  • Dominic Scaglioni
  • , Francesco Catapano
  • , Matthew Ellis
  • , Silvia Torelli
  • , Darren Chambers
  • , Lucy Feng
  • , Matthew Beck
  • , Caroline Sewry
  • , Mauro Monforte
  • , Shawn Harriman
  • , Erica Koenig
  • , Jyoti Malhotra
  • , Linda Popplewell
  • , Michela Guglieri
  • , Volker Straub
  • , Eugenio Mercuri
  • , Laurent Servais
  • , Rahul Phadke
  • , Jennifer Morgan
  • , Francesco Muntoni

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Article number7
JournalActa Neuropathologica
Volume9
DOIs
Publication statusPublished - 6 Jan 2021

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