Systemic Intravenous Administration of Antisense Therapeutics for Combinatorial Dystrophin and Myostatin Exon Splice Modulation

Ngoc Lu-Nguyen; George Dickson; Alberto Malerba

doi:10.1007/978-1-4939-8651-4_21

Systemic Intravenous Administration of Antisense Therapeutics for Combinatorial Dystrophin and Myostatin Exon Splice Modulation

Ngoc Lu-Nguyen, George Dickson, Alberto Malerba

Research output: Contribution to journal › Article › peer-review

Original language	English
Pages (from-to)	343-354
Number of pages	12
Journal	Methods in Molecular Biology
Volume	1828
DOIs	https://doi.org/10.1007/978-1-4939-8651-4_21
Publication status	E-pub ahead of print - 1 Sept 2018

Keywords

Journal Article

Access to Document

10.1007/978-1-4939-8651-4_21

Destructive Exon Skipping of Myostatin mRNA with and without Open Reading Frame Rescue of Dystrophin
Lu-Nguyen, N. (Researcher) & Dickson, G. (PI)
Industrial
1/01/14 → 30/06/15
Project: Research
Combination Antisense Treatment for Duchenne Muscular Dystrophy: Open Reading Frame Rescue of Dystrophin in conjunction with Destructive Exon Skipping of Myostatin mRNA
Lu-Nguyen, N. (Researcher) & Dickson, G. (PI)
Muscular Dystrophy Campaign
1/02/12 → 31/08/15
Project: Research

Hellenic Society of Gene Therapy and Regenerative Medicine Congress (Greece)
Lu-Nguyen, N. (Speaker)
2016
Activity: Talk or presentation › Oral presentation
Workshop on delivery and delivery to the central nervous system (Spain)
Lu-Nguyen, N. (Speaker)
2016
Activity: Talk or presentation › Oral presentation
Training school on patient communication (Netherlands)
Lu-Nguyen, N. (Speaker)
2015
Activity: Talk or presentation › Oral presentation

Travel Grant - British Society for Gene and Cell Therapy
Lu-Nguyen, N. (Recipient), 2016
Prize: Prize (including medals and awards)

Cite this

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title = "Systemic Intravenous Administration of Antisense Therapeutics for Combinatorial Dystrophin and Myostatin Exon Splice Modulation",

keywords = "Journal Article",

author = "Ngoc Lu-Nguyen and George Dickson and Alberto Malerba",

year = "2018",

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day = "1",

doi = "10.1007/978-1-4939-8651-4_21",

language = "English",

volume = "1828",

pages = "343--354",

journal = "Methods in Molecular Biology",

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T1 - Systemic Intravenous Administration of Antisense Therapeutics for Combinatorial Dystrophin and Myostatin Exon Splice Modulation

AU - Lu-Nguyen, Ngoc

AU - Dickson, George

AU - Malerba, Alberto

PY - 2018/9/1

Y1 - 2018/9/1

KW - Journal Article

U2 - 10.1007/978-1-4939-8651-4_21

DO - 10.1007/978-1-4939-8651-4_21

M3 - Article

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SN - 1064-3745

VL - 1828

SP - 343

EP - 354

JO - Methods in Molecular Biology

JF - Methods in Molecular Biology

ER -

Systemic Intravenous Administration of Antisense Therapeutics for Combinatorial Dystrophin and Myostatin Exon Splice Modulation

Keywords

Access to Document

Projects

Destructive Exon Skipping of Myostatin mRNA with and without Open Reading Frame Rescue of Dystrophin

Combination Antisense Treatment for Duchenne Muscular Dystrophy: Open Reading Frame Rescue of Dystrophin in conjunction with Destructive Exon Skipping of Myostatin mRNA

Activities

Hellenic Society of Gene Therapy and Regenerative Medicine Congress (Greece)

Workshop on delivery and delivery to the central nervous system (Spain)

Training school on patient communication (Netherlands)

Prizes

Travel Grant - British Society for Gene and Cell Therapy

Cite this