Systemic antisense therapeutics inhibiting DUX4 expression ameliorates FSHD-like pathology in an FSHD mouse model

Ngoc Lu-Nguyen, Alberto Malerba, Shan Herath, George Dickson, Linda Popplewell

Research output: Contribution to journalArticlepeer-review

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Original languageEnglish
Article numberddab136
Pages (from-to)1398-1412
Number of pages15
JournalHuman Molecular Genetics
Volume30
Issue number15
Early online date13 May 2021
DOIs
Publication statusPublished - 1 Aug 2021

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