Stable micro-dystrophin gene transfer using an integrating adeno-retroviral hybrid vector ameliorates the dystrophic pathology in mdx mouse muscle

Michael L Roberts, Dominic J Wells, Ian R Graham, Stewart A Fabb, Vanessa J Hill, Ghislaine Duisit, Katsutoshi Yuasa, Shin'ichi Takeda, François-Loïc Cosset, George Dickson

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)1719-30
Number of pages12
JournalHuman Molecular Genetics
Issue number15
Publication statusPublished - 2002


  • Adenoviridae
  • Animals
  • Disease Models, Animal
  • Dystrophin
  • Gene Therapy
  • Gene Transfer Techniques
  • Genetic Vectors
  • Lac Operon
  • Mice
  • Mice, Inbred mdx
  • Mice, Transgenic
  • Muscle, Skeletal
  • Muscular Dystrophy, Duchenne
  • Retroviridae
  • Transduction, Genetic

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