PABPN1 gene therapy for oculopharyngeal muscular dystrophy

A Malerba; P Klein; Houria Bachtarzi; S A Jarmin; G Cordova; A Ferry; V Strings; M Polay Espinoza; K Mamchaoui; S C Blumen; J Lacau St Guily; V Mouly; M Graham; G Butler-Browne; D A Suhy; C Trollet; George Dickson

doi:10.1038/ncomms14848

PABPN1 gene therapy for oculopharyngeal muscular dystrophy

A Malerba, P Klein, Houria Bachtarzi, S A Jarmin, G Cordova, A Ferry, V Strings, M Polay Espinoza, K Mamchaoui, S C Blumen, J Lacau St Guily, V Mouly, M Graham, G Butler-Browne, D A Suhy, C Trollet, George Dickson

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Original language	English
Article number	14848
Pages (from-to)	1-14
Number of pages	14
Journal	Nature Communications
Volume	8
DOIs	https://doi.org/10.1038/ncomms14848
Publication status	Published - 31 Mar 2017

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Journal Article

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10.1038/ncomms14848Licence: CC BY

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Malerba, A., Klein, P., Bachtarzi, H., Jarmin, S. A., Cordova, G., Ferry, A., Strings, V., Espinoza, M. P., Mamchaoui, K., Blumen, S. C., St Guily, J. L., Mouly, V., Graham, M., Butler-Browne, G., Suhy, D. A., Trollet, C., & Dickson, G. (2017). PABPN1 gene therapy for oculopharyngeal muscular dystrophy. Nature Communications, 8, 1-14. Article 14848. https://doi.org/10.1038/ncomms14848

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AU - Ferry, A

AU - Strings, V

AU - Espinoza, M Polay

AU - Mamchaoui, K

AU - Blumen, S C

AU - St Guily, J Lacau

AU - Mouly, V

AU - Graham, M

AU - Butler-Browne, G

AU - Suhy, D A

AU - Trollet, C

AU - Dickson, George

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