Optimisation of lentiviral vectors for gene therapy of spinal muscular atrophy

Neda Ali Mohammadi Nafchi

Research output: ThesisDoctoral Thesis

429 Downloads (Pure)
Original languageEnglish
Awarding Institution
  • Royal Holloway, University of London
  • Yáñez-Muñoz, Rafael J., Supervisor
  • Chen, Philip, Advisor
Thesis sponsors
Award date1 Sept 2017
Publication statusUnpublished - 2017


  • Biomedical science
  • Gene therapy
  • Gene addition
  • Lentiviral vectors
  • In utero
  • Spinal muscular atrophy
  • Survival motor neuron gene

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