Long-Term Systemic Treatment of a Mouse Model Displaying Chronic FSHD-like Pathology with Antisense Therapeutics That Inhibit DUX4 Expression

Ngoc Lu-Nguyen; George Dickson; Alberto Malerba; Linda Popplewell

doi:10.3390/biomedicines10071623

Long-Term Systemic Treatment of a Mouse Model Displaying Chronic FSHD-like Pathology with Antisense Therapeutics That Inhibit DUX4 Expression

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Original language	English
Article number	1623
Journal	Biomedicines
Volume	10
Issue number	7
DOIs	https://doi.org/10.3390/biomedicines10071623
Publication status	Published - 7 Jul 2022

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10.3390/biomedicines10071623Licence: CC BY

2022 Lu-Nguyen and Popplewell. Long-term systemic antisense treatment in chronic FSHD miceLicence: CC BY

https://www.mdpi.com/2227-9059/10/7/1623/htm

Development of cell-penetrating peptide-conjugated antisense oligonucleotides for the treatment of Fascioscapulohumeral Muscular Dystrophy
Lu-Nguyen, N. (Researcher), Dickson, G. (CoPI) & Popplewell, L. (PI)
Muscular Dystrophy UK
1/10/16 → 31/10/18
Project: Research

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title = "Long-Term Systemic Treatment of a Mouse Model Displaying Chronic FSHD-like Pathology with Antisense Therapeutics That Inhibit DUX4 Expression",

author = "Ngoc Lu-Nguyen and George Dickson and Alberto Malerba and Linda Popplewell",

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AU - Lu-Nguyen, Ngoc

AU - Dickson, George

AU - Malerba, Alberto

AU - Popplewell, Linda

PY - 2022/7/7

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Long-Term Systemic Treatment of a Mouse Model Displaying Chronic FSHD-like Pathology with Antisense Therapeutics That Inhibit DUX4 Expression

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Projects

Development of cell-penetrating peptide-conjugated antisense oligonucleotides for the treatment of Fascioscapulohumeral Muscular Dystrophy

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