Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy

Caroline Le Guiner; Laurent Servais; Marie Montus; Thibaut Larcher; Bodvaël Fraysse; Sophie Moullec; Marine Allais; Virginie François; Maeva Dutilleul; Alberto Malerba; Taeyoung Koo; Jean-Laurent Thibaut; Béatrice Matot; Marie Devaux; Johanne Le Duff; Jack-Yves Deschamps; Inès Barthelemy; Stéphane Blot; Isabelle Testault; Karim Wahbi; Stéphane Ederhy; Samia Martin; Philippe Veron; Christophe Georger; Takis Athanasopoulos; Carole Masurier; Federico Mingozzi; Pierre Carlier; Bernard Gjata; Jean-Yves Hogrel; Oumeya Adjali; Fulvio Mavilio; Thomas Voit; Philippe Moullier; George Dickson

doi:10.1038/ncomms16105

Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy

Caroline Le Guiner, Laurent Servais, Marie Montus, Thibaut Larcher, Bodvaël Fraysse, Sophie Moullec, Marine Allais, Virginie François, Maeva Dutilleul, Alberto Malerba, Taeyoung Koo, Jean-Laurent Thibaut, Béatrice Matot, Marie Devaux, Johanne Le Duff, Jack-Yves Deschamps, Inès Barthelemy, Stéphane Blot, Isabelle Testault, Karim WahbiStéphane Ederhy, Samia Martin, Philippe Veron, Christophe Georger, Takis Athanasopoulos, Carole Masurier, Federico Mingozzi, Pierre Carlier, Bernard Gjata, Jean-Yves Hogrel, Oumeya Adjali, Fulvio Mavilio, Thomas Voit, Philippe Moullier, George Dickson

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Original language	English
Article number	16105
Pages (from-to)	1-15
Number of pages	15
Journal	Nature Communications
Volume	8
DOIs	https://doi.org/10.1038/ncomms16105
Publication status	Published - 25 Jul 2017

Keywords

Journal Article

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10.1038/ncomms16105Licence: CC BY

Final ManuscriptFinal published version, 2.15 MBLicence: CC BY

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Le Guiner, C., Servais, L., Montus, M., Larcher, T., Fraysse, B., Moullec, S., Allais, M., François, V., Dutilleul, M., Malerba, A., Koo, T., Thibaut, J.-L., Matot, B., Devaux, M., Le Duff, J., Deschamps, J.-Y., Barthelemy, I., Blot, S., Testault, I., ... Dickson, G. (2017). Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy. Nature Communications, 8, 1-15. Article 16105. https://doi.org/10.1038/ncomms16105

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title = "Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy",

keywords = "Journal Article",

author = "{Le Guiner}, Caroline and Laurent Servais and Marie Montus and Thibaut Larcher and Bodva{\"e}l Fraysse and Sophie Moullec and Marine Allais and Virginie Fran{\c c}ois and Maeva Dutilleul and Alberto Malerba and Taeyoung Koo and Jean-Laurent Thibaut and B{\'e}atrice Matot and Marie Devaux and {Le Duff}, Johanne and Jack-Yves Deschamps and In{\`e}s Barthelemy and St{\'e}phane Blot and Isabelle Testault and Karim Wahbi and St{\'e}phane Ederhy and Samia Martin and Philippe Veron and Christophe Georger and Takis Athanasopoulos and Carole Masurier and Federico Mingozzi and Pierre Carlier and Bernard Gjata and Jean-Yves Hogrel and Oumeya Adjali and Fulvio Mavilio and Thomas Voit and Philippe Moullier and George Dickson",

year = "2017",

month = jul,

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doi = "10.1038/ncomms16105",

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Le Guiner, C, Servais, L, Montus, M, Larcher, T, Fraysse, B, Moullec, S, Allais, M, François, V, Dutilleul, M, Malerba, A, Koo, T, Thibaut, J-L, Matot, B, Devaux, M, Le Duff, J, Deschamps, J-Y, Barthelemy, I, Blot, S, Testault, I, Wahbi, K, Ederhy, S, Martin, S, Veron, P, Georger, C, Athanasopoulos, T, Masurier, C, Mingozzi, F, Carlier, P, Gjata, B, Hogrel, J-Y, Adjali, O, Mavilio, F, Voit, T, Moullier, P & Dickson, G 2017, 'Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy', Nature Communications, vol. 8, 16105, pp. 1-15. https://doi.org/10.1038/ncomms16105

TY - JOUR

T1 - Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy

AU - Le Guiner, Caroline

AU - Servais, Laurent

AU - Montus, Marie

AU - Larcher, Thibaut

AU - Fraysse, Bodvaël

AU - Moullec, Sophie

AU - Allais, Marine

AU - François, Virginie

AU - Dutilleul, Maeva

AU - Malerba, Alberto

AU - Koo, Taeyoung

AU - Thibaut, Jean-Laurent

AU - Matot, Béatrice

AU - Devaux, Marie

AU - Le Duff, Johanne

AU - Deschamps, Jack-Yves

AU - Barthelemy, Inès

AU - Blot, Stéphane

AU - Testault, Isabelle

AU - Wahbi, Karim

AU - Ederhy, Stéphane

AU - Martin, Samia

AU - Veron, Philippe

AU - Georger, Christophe

AU - Athanasopoulos, Takis

AU - Masurier, Carole

AU - Mingozzi, Federico

AU - Carlier, Pierre

AU - Gjata, Bernard

AU - Hogrel, Jean-Yves

AU - Adjali, Oumeya

AU - Mavilio, Fulvio

AU - Voit, Thomas

AU - Moullier, Philippe

AU - Dickson, George

PY - 2017/7/25

Y1 - 2017/7/25

KW - Journal Article

U2 - 10.1038/ncomms16105

DO - 10.1038/ncomms16105

M3 - Article

C2 - 28742067

SN - 2041-1723

VL - 8

SP - 1

EP - 15

JO - Nature Communications

JF - Nature Communications

M1 - 16105

ER -