@article{be4130b031354732951af084af667c1b,
title = "Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-escalation, proof-of-concept study",
keywords = "Adolescent, Child, Dose-Response Relationship, Drug, Dystrophin, Gene Therapy, Humans, Immunohistochemistry, Male, Muscle, Skeletal, Muscular Dystrophy, Duchenne, Oligonucleotides, Reverse Transcriptase Polymerase Chain Reaction, Single-Blind Method",
author = "Maria Kinali and Virginia Arechavala-Gomeza and Lucy Feng and Sebahattin Cirak and David Hunt and Carl Adkin and Michela Guglieri and Emma Ashton and Stephen Abbs and Petros Nihoyannopoulos and Garralda, \{Maria Elena\} and Mary Rutherford and Caroline McCulley and Linda Popplewell and Graham, \{Ian R\} and George Dickson and Wood, \{Matthew J A\} and Wells, \{Dominic J\} and Wilton, \{Steve D\} and Ryszard Kole and Volker Straub and Kate Bushby and Caroline Sewry and Morgan, \{Jennifer E\} and Francesco Muntoni",
year = "2009",
month = oct,
doi = "10.1016/S1474-4422(09)70211-X",
language = "English",
volume = "8",
pages = "918--928",
journal = "Lancet Neurology",
issn = "1474-4422",
publisher = "Elsevier Ltd",
number = "10",
}