Improving molecular and histopathology in diaphragm muscle of the double transgenic ACTA1-MCM/FLExDUX4 mouse model of FSHD with systemic antisense therapy

Ngoc Lu-Nguyen; Alberto Malerba; Marina Antoni Pineda; George Dickson; Linda J Popplewell

doi:10.1089/hum.2021.251

Improving molecular and histopathology in diaphragm muscle of the double transgenic ACTA1-MCM/FLExDUX4 mouse model of FSHD with systemic antisense therapy

Ngoc Lu-Nguyen
, Alberto Malerba
, Marina Antoni Pineda
, George Dickson
, Linda J Popplewell

Research output: Contribution to journal › Article › peer-review

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Original language	English
Pages (from-to)	923-935
Number of pages	13
Journal	Human Gene Therapy
Volume	33
Issue number	17-18
Early online date	28 Apr 2022
DOIs	https://doi.org/10.1089/hum.2021.251
Publication status	Published - 16 Sept 2022

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10.1089/hum.2021.251

Accepted ManuscriptAccepted author manuscript, 1.32 MB

Cite this

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title = "Improving molecular and histopathology in diaphragm muscle of the double transgenic ACTA1-MCM/FLExDUX4 mouse model of FSHD with systemic antisense therapy",

author = "Ngoc Lu-Nguyen and Alberto Malerba and \{Antoni Pineda\}, Marina and George Dickson and Popplewell, \{Linda J\}",

year = "2022",

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doi = "10.1089/hum.2021.251",

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AU - Lu-Nguyen, Ngoc

AU - Malerba, Alberto

AU - Antoni Pineda, Marina

AU - Dickson, George

AU - Popplewell, Linda J

PY - 2022/9/16

Y1 - 2022/9/16

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DO - 10.1089/hum.2021.251

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SN - 1043-0342

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JO - Human Gene Therapy

JF - Human Gene Therapy

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