Improving molecular and histopathology in diaphragm muscle of the double transgenic ACTA1-MCM/FLExDUX4 mouse model of FSHD with systemic antisense therapy

Ngoc Lu-Nguyen, Alberto Malerba, Marina Antoni Pineda, George Dickson, Linda J Popplewell

Research output: Contribution to journalArticlepeer-review

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Original languageEnglish
Pages (from-to)923-935
Number of pages13
JournalHuman Gene Therapy
Issue number17-18
Early online date28 Apr 2022
Publication statusPublished - 16 Sept 2022

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