Gene therapy for spinal muscular atrophy: perspectives on the possibility of optimizing SMN1 delivery to correct all neurological and systemic perturbations

Sharon Brown; R. J. Yáñez-Muñoz; Heidi R. Fuller

doi:10.4103/NRR.NRR-D-24-00504

Gene therapy for spinal muscular atrophy: perspectives on the possibility of optimizing SMN1 delivery to correct all neurological and systemic perturbations

Sharon Brown, R. J. Yáñez-Muñoz, Heidi R. Fuller

Research output: Contribution to journal › Review article › peer-review

Original language	English
Journal	Neural Regeneration Research
DOIs	https://doi.org/10.4103/NRR.NRR-D-24-00504
Publication status	Published - 29 Jul 2024

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10.4103/NRR.NRR-D-24-00504

Cite this

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title = "Gene therapy for spinal muscular atrophy: perspectives on the possibility of optimizing SMN1 delivery to correct all neurological and systemic perturbations",

author = "Sharon Brown and Y{\'a}{\~n}ez-Mu{\~n}oz, {R. J.} and Fuller, {Heidi R.}",

year = "2024",

month = jul,

day = "29",

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language = "English",

journal = "Neural Regeneration Research",

issn = "1876-7958",

publisher = "Wolters Kluwer Medknow Publications",

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T1 - Gene therapy for spinal muscular atrophy: perspectives on the possibility of optimizing SMN1 delivery to correct all neurological and systemic perturbations

AU - Brown, Sharon

AU - Yáñez-Muñoz, R. J.

AU - Fuller, Heidi R.

PY - 2024/7/29

Y1 - 2024/7/29

U2 - 10.4103/NRR.NRR-D-24-00504

DO - 10.4103/NRR.NRR-D-24-00504

M3 - Review article

SN - 1876-7958

JO - Neural Regeneration Research

JF - Neural Regeneration Research

ER -