Gene Therapy for Duchenne Muscular Dystrophy: Engineering microdystrophin expressing cassettes from recombinant adeno-associated virus for improved clinical efficacy

Nertiyan Elangkovan

Research output: ThesisDoctoral Thesis

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Original languageEnglish
QualificationPh.D.
Awarding Institution
  • Royal Holloway, University of London
Supervisors/Advisors
  • Popplewell, Linda, Supervisor
  • Dickson, George, Supervisor
Award date1 Oct 2021
Publication statusUnpublished - 2021

Keywords

  • AAV vector
  • Gene Therapy
  • Duchenne muscular dystrophy
  • microdystrophin

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