Gene editing targeting the AAVS1 site for site specific integration of microdystrophin for treatment of Duchenne Muscular Dystrophy

Research output: Thesis › Doctoral Thesis

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Original language	English
Qualification	Ph.D.
Awarding Institution	Royal Holloway, University of London
Supervisors/Advisors	Popplewell, Linda, Supervisor Malerba, Alberto, Supervisor Yáñez-Muñoz, Rafael J., Advisor
Thesis sponsors	Royal Holloway University of London
Award date	1 Dec 2023
Publication status	Unpublished - 2023

Keywords

@phdthesis{eb5150be3acd4c1bbf5a43efc4c87fac,

title = "Gene editing targeting the AAVS1 site for site specific integration of microdystrophin for treatment of Duchenne Muscular Dystrophy",

keywords = "Gene therapy, Gene editing, Duchenne muscular dystrophy, CRISPR/Cas9",

author = "Arjun Agarwal",

year = "2023",

language = "English",

school = "Royal Holloway, University of London",

}