Established PABPN1 intranuclear inclusions in OPMD muscle can be efficiently reversed by AAV-mediated knock-down and replacement of mutant expanded PABPN1

  • Alberto Malerba
  • , Pierre Klein
  • , Ngoc Lu-Nguyen
  • , Ornella Cappellari
  • , Vanessa Strings-Ufombah
  • , Sonal Harbaran
  • , Peter Roelvink
  • , David Suhy
  • , Capucine Trollet
  • , George Dickson

Research output: Contribution to journal › Article › peer-review

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