Comparative analysis of antisense oligonucleotide sequences targeting exon 53 of the human DMD gene: Implications for future clinical trials

Linda J Popplewell, Carl Adkin, Virginia Arechavala-Gomeza, Annemieke Aartsma-Rus, Christa L de Winter, Steve D Wilton, Jennifer E Morgan, Francesco Muntoni, Ian R Graham, George Dickson

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)102-10
Number of pages9
JournalNeuromuscular disorders
Issue number2
Publication statusPublished - 2010


  • Animals
  • Base Sequence
  • Cells, Cultured
  • Disease Models, Animal
  • Dystrophin
  • Exons
  • Gene Expression Regulation
  • Gene Targeting
  • Gene Therapy
  • Humans
  • Male
  • Mice
  • Mice, Transgenic
  • Morpholines
  • Muscular Dystrophy, Duchenne
  • Mutation
  • Oligonucleotides, Antisense
  • Transcription, Genetic

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