Comparative analysis of antisense oligonucleotide sequences for targeted skipping of Exon 51 during dystrophin Pre-mRNA splicing in human muscle

V. Arechavala-Gomeza; I. R. Graham; L. J. Popplewell; A. M. Adams; A. Aartsma-Rus; M. Kinali; J. E. Morgan; J. C. Van Deutekom; S. D. Wilton; G. Dickson; F. Muntoni

doi:10.1089/hum.2006.061

Comparative analysis of antisense oligonucleotide sequences for targeted skipping of Exon 51 during dystrophin Pre-mRNA splicing in human muscle

V. Arechavala-Gomeza
, I. R. Graham
, L. J. Popplewell
, A. M. Adams
, A. Aartsma-Rus
, M. Kinali
, J. E. Morgan
, J. C. Van Deutekom
, S. D. Wilton
, G. Dickson
, F. Muntoni

Research output: Contribution to journal › Article › peer-review

Original language	English
Pages (from-to)	798-810
Number of pages	13
Journal	Human Gene Therapy
Volume	18
Issue number	9
DOIs	https://doi.org/10.1089/hum.2006.061
Publication status	Published - Sept 2007

Keywords

DUCHENNE MUSCULAR-DYSTROPHY
MDX MOUSE MUSCLE
NONSENSE MUTATION
SOMATIC REVERSION
SYSTEMIC DELIVERY
REVERTANT FIBERS
GENE TRANSCRIPT
POSITIVE FIBERS
IN-VITRO
EXPRESSION

Access to Document

10.1089/hum.2006.061

Cite this

Arechavala-Gomeza, V., Graham, I. R., Popplewell, L. J., Adams, A. M., Aartsma-Rus, A., Kinali, M., Morgan, J. E., Van Deutekom, J. C., Wilton, S. D., Dickson, G., & Muntoni, F. (2007). Comparative analysis of antisense oligonucleotide sequences for targeted skipping of Exon 51 during dystrophin Pre-mRNA splicing in human muscle. Human Gene Therapy, 18(9), 798-810. https://doi.org/10.1089/hum.2006.061

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title = "Comparative analysis of antisense oligonucleotide sequences for targeted skipping of Exon 51 during dystrophin Pre-mRNA splicing in human muscle",

keywords = "DUCHENNE MUSCULAR-DYSTROPHY, MDX MOUSE MUSCLE, NONSENSE MUTATION, SOMATIC REVERSION, SYSTEMIC DELIVERY, REVERTANT FIBERS, GENE TRANSCRIPT, POSITIVE FIBERS, IN-VITRO, EXPRESSION",

author = "V. Arechavala-Gomeza and Graham, \{I. R.\} and Popplewell, \{L. J.\} and Adams, \{A. M.\} and A. Aartsma-Rus and M. Kinali and Morgan, \{J. E.\} and \{Van Deutekom\}, \{J. C.\} and Wilton, \{S. D.\} and G. Dickson and F. Muntoni",

year = "2007",

month = sep,

doi = "10.1089/hum.2006.061",

language = "English",

volume = "18",

pages = "798--810",

journal = "Human Gene Therapy",

issn = "1043-0342",

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Arechavala-Gomeza, V, Graham, IR, Popplewell, LJ, Adams, AM, Aartsma-Rus, A, Kinali, M, Morgan, JE, Van Deutekom, JC, Wilton, SD, Dickson, G & Muntoni, F 2007, 'Comparative analysis of antisense oligonucleotide sequences for targeted skipping of Exon 51 during dystrophin Pre-mRNA splicing in human muscle', Human Gene Therapy, vol. 18, no. 9, pp. 798-810. https://doi.org/10.1089/hum.2006.061

TY - JOUR

T1 - Comparative analysis of antisense oligonucleotide sequences for targeted skipping of Exon 51 during dystrophin Pre-mRNA splicing in human muscle

AU - Arechavala-Gomeza, V.

AU - Graham, I. R.

AU - Popplewell, L. J.

AU - Adams, A. M.

AU - Aartsma-Rus, A.

AU - Kinali, M.

AU - Morgan, J. E.

AU - Van Deutekom, J. C.

AU - Wilton, S. D.

AU - Dickson, G.

AU - Muntoni, F.

PY - 2007/9

Y1 - 2007/9

KW - DUCHENNE MUSCULAR-DYSTROPHY

KW - MDX MOUSE MUSCLE

KW - NONSENSE MUTATION

KW - SOMATIC REVERSION

KW - SYSTEMIC DELIVERY

KW - REVERTANT FIBERS

KW - GENE TRANSCRIPT

KW - POSITIVE FIBERS

KW - IN-VITRO

KW - EXPRESSION

U2 - 10.1089/hum.2006.061

DO - 10.1089/hum.2006.061

M3 - Article

SN - 1043-0342

VL - 18

SP - 798

EP - 810

JO - Human Gene Therapy

JF - Human Gene Therapy

IS - 9

ER -