Combination antisense treatment for destructive exon skipping of myostatin and open reading frame rescue of dystrophin in neonatal mdx mice

Ngoc Lu-Nguyen; Susan A Jarmin; Amer F Saleh; Linda Popplewell; Michael J Gait; George Dickson

doi:10.1038/mt.2015.88

Combination antisense treatment for destructive exon skipping of myostatin and open reading frame rescue of dystrophin in neonatal mdx mice

Ngoc Lu-Nguyen
, Susan A Jarmin
, Amer F Saleh
, Linda Popplewell
, Michael J Gait
, George Dickson

Research output: Contribution to journal › Article › peer-review

172 Downloads (Pure)

Original language	English
Pages (from-to)	1341-1348
Number of pages	8
Journal	Molecular Therapy
Volume	23
Issue number	8
DOIs	https://doi.org/10.1038/mt.2015.88
Publication status	Published - Aug 2015

Access to Document

10.1038/mt.2015.88

Accepted ManuscriptAccepted author manuscript, 3.66 MBLicence: CC BY-NC-ND

http://www.nature.com/mt/journal/vaop/naam/abs/mt201588a.html

Combination Antisense Treatment for Duchenne Muscular Dystrophy: Open Reading Frame Rescue of Dystrophin in conjunction with Destructive Exon Skipping of Myostatin mRNA
Lu-Nguyen, N. (Researcher) & Dickson, G. (PI)
Muscular Dystrophy Campaign
1/02/12 → 31/08/15
Project: Research

Workshop on delivery and delivery to the central nervous system (Spain)
Lu-Nguyen, N. (Speaker)
2016
Activity: Talk, presentation or media contribution › Oral presentation
Hellenic Society of Gene Therapy and Regenerative Medicine Congress (Greece)
Lu-Nguyen, N. (Speaker)
2016
Activity: Talk, presentation or media contribution › Oral presentation
8th Annual Neuromuscular Translational Research Conference (UK)
Lu-Nguyen, N. (Speaker)
2015
Activity: Talk, presentation or media contribution › Oral presentation

Travel Grant - Oligonucleotide Therapeutics Society (USA)
Lu-Nguyen, N. (Recipient), 2014
Prize: Prize (including medals and awards)

Cite this

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title = "Combination antisense treatment for destructive exon skipping of myostatin and open reading frame rescue of dystrophin in neonatal mdx mice",

author = "Ngoc Lu-Nguyen and Jarmin, \{Susan A\} and Saleh, \{Amer F\} and Linda Popplewell and Gait, \{Michael J\} and George Dickson",

year = "2015",

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doi = "10.1038/mt.2015.88",

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journal = "Molecular Therapy",

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T1 - Combination antisense treatment for destructive exon skipping of myostatin and open reading frame rescue of dystrophin in neonatal mdx mice

AU - Lu-Nguyen, Ngoc

AU - Jarmin, Susan A

AU - Saleh, Amer F

AU - Popplewell, Linda

AU - Gait, Michael J

AU - Dickson, George

PY - 2015/8

Y1 - 2015/8

U2 - 10.1038/mt.2015.88

DO - 10.1038/mt.2015.88

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SN - 1525-0016

VL - 23

SP - 1341

EP - 1348

JO - Molecular Therapy

JF - Molecular Therapy

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Combination antisense treatment for destructive exon skipping of myostatin and open reading frame rescue of dystrophin in neonatal mdx mice

Access to Document

Projects

Combination Antisense Treatment for Duchenne Muscular Dystrophy: Open Reading Frame Rescue of Dystrophin in conjunction with Destructive Exon Skipping of Myostatin mRNA

Activities

Workshop on delivery and delivery to the central nervous system (Spain)

Hellenic Society of Gene Therapy and Regenerative Medicine Congress (Greece)

8th Annual Neuromuscular Translational Research Conference (UK)

Prizes

Travel Grant - Oligonucleotide Therapeutics Society (USA)

Cite this