Combination antisense treatment for destructive exon skipping of myostatin and open reading frame rescue of dystrophin in neonatal mdx mice

Ngoc Lu-Nguyen; Susan A Jarmin; Amer F Saleh; Linda Popplewell; Michael J Gait; George Dickson

doi:10.1038/mt.2015.88

Combination antisense treatment for destructive exon skipping of myostatin and open reading frame rescue of dystrophin in neonatal mdx mice

Ngoc Lu-Nguyen, Susan A Jarmin, Amer F Saleh, Linda Popplewell, Michael J Gait, George Dickson

Research output: Contribution to journal › Article › peer-review

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Original language	English
Pages (from-to)	1341-1348
Number of pages	8
Journal	Molecular Therapy
Volume	23
Issue number	8
DOIs	https://doi.org/10.1038/mt.2015.88
Publication status	Published - Aug 2015

Access to Document

10.1038/mt.2015.88

Accepted ManuscriptAccepted author manuscript, 3.66 MBLicence: CC BY-NC-ND

http://www.nature.com/mt/journal/vaop/naam/abs/mt201588a.html

Combination Antisense Treatment for Duchenne Muscular Dystrophy: Open Reading Frame Rescue of Dystrophin in conjunction with Destructive Exon Skipping of Myostatin mRNA
Lu-Nguyen, N. (Researcher) & Dickson, G. (PI)
Muscular Dystrophy Campaign
1/02/12 → 31/08/15
Project: Research

Hellenic Society of Gene Therapy and Regenerative Medicine Congress (Greece)
Lu-Nguyen, N. (Speaker)
2016
Activity: Talk or presentation › Oral presentation
Workshop on delivery and delivery to the central nervous system (Spain)
Lu-Nguyen, N. (Speaker)
2016
Activity: Talk or presentation › Oral presentation
Training school on patient communication (Netherlands)
Lu-Nguyen, N. (Speaker)
2015
Activity: Talk or presentation › Oral presentation

Travel Grant - Oligonucleotide Therapeutics Society (USA)
Lu-Nguyen, N. (Recipient), 2014
Prize: Prize (including medals and awards)

Cite this

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title = "Combination antisense treatment for destructive exon skipping of myostatin and open reading frame rescue of dystrophin in neonatal mdx mice",

author = "Ngoc Lu-Nguyen and Jarmin, {Susan A} and Saleh, {Amer F} and Linda Popplewell and Gait, {Michael J} and George Dickson",

year = "2015",

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AU - Lu-Nguyen, Ngoc

AU - Jarmin, Susan A

AU - Saleh, Amer F

AU - Popplewell, Linda

AU - Gait, Michael J

AU - Dickson, George

PY - 2015/8

Y1 - 2015/8

U2 - 10.1038/mt.2015.88

DO - 10.1038/mt.2015.88

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SP - 1341

EP - 1348

JO - Molecular Therapy

JF - Molecular Therapy

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Combination antisense treatment for destructive exon skipping of myostatin and open reading frame rescue of dystrophin in neonatal mdx mice

Access to Document

Projects

Combination Antisense Treatment for Duchenne Muscular Dystrophy: Open Reading Frame Rescue of Dystrophin in conjunction with Destructive Exon Skipping of Myostatin mRNA

Activities

Hellenic Society of Gene Therapy and Regenerative Medicine Congress (Greece)

Workshop on delivery and delivery to the central nervous system (Spain)

Training school on patient communication (Netherlands)

Prizes

Travel Grant - Oligonucleotide Therapeutics Society (USA)

Cite this