Centre of Gene and Cell Therapy

Research output

Research output per year 2010 2010 2011 2012 2013 2014 2015 2016 2017 2018 2019 2023 2024 2024

• 186 Article
• 19 Doctoral Thesis
• 11 Conference contribution
• 10 Review article
• 36 More
  • 6 Editorial
  • 5 Chapter
  • 4 Book/Film/Article review
  • 3 Book
  • 3 Entry for encyclopedia/dictionary
  • 3 Chapter (peer-reviewed)
  • 3 Other contribution
  • 2 Abstract
  • 2 Meeting abstract
  • 2 Literature review
  • 1 Comment/debate
  • 1 Web publication/site
  • 1 Patent

Research output per year

Research output per year

Search results

• 2024

  Gene therapy for spinal muscular atrophy: perspectives on the possibility of optimizing SMN1 delivery to correct all neurological and systemic perturbations

  Brown, S., Yáñez-Muñoz, R. J. & Fuller, H. R., 29 Jul 2024, In: Neural Regeneration Research.

  Research output: Contribution to journal › Review article › peer-review

  Open Access
• 2023

  Clinical applications of gene therapy for rare diseases: a review

  Papaioannou, I., Owen, J. S. & Yáñez-Muñoz, R. J., 13 May 2023, In: International Journal of Experimental Pathology. 104, p. 154–176

  Research output: Contribution to journal › Review article › peer-review

• Foes to friends: do pathogens hold the key to gene therapy?

  Pearson, M. & Yáñez-Muñoz, R. J., 21 Aug 2023, In: Biochemist. 45, 4, p. 15-22 8 p.

  Research output: Contribution to journal › Review article

  Open Access

• Spinal Muscular Atrophy: A Rare but Treatable Disease of the Nervous System

  Sleigh, J. N., Christie-Brown, V., Ryburn, L. & Yáñez-Muñoz, R. J., 1 Aug 2023, In: Frontiers for Young Minds.

  Research output: Contribution to journal › Review article › peer-review

  Open Access

• The British Society for Gene and Cell Therapy at 20 (2003-2023)

  Seymour, L., Thrasher, A., Baker, A., Griesenbach, U. & Yáñez-Muñoz, R. J., 22 Nov 2023, (Accepted/In press) In: Human Gene Therapy.

  Research output: Contribution to journal › Review article › peer-review

  Open Access

  File
  30 Downloads (Pure)
• 2018

  Synaptic dysfunction in Alzheimer's disease: the effects of amyloid beta on synaptic vesicle dynamics as a novel target for therapeutic intervention

  Marsh, J. & Alifragis, P., 27 Apr 2018, (E-pub ahead of print) In: Neural Regeneration Research. 13, 4, p. 616-623 8 p.

  Research output: Contribution to journal › Review article › peer-review

  Open Access
• 2017

  Nonintegrating Gene Therapy Vectors

  Athanasopoulos, T., Munye, M. M. & Yáñez-Muñoz, R. J., Oct 2017, In: Hematology/Oncology Clinics of North America. 31, 5, p. 753-770 18 p.

  Research output: Contribution to journal › Review article › peer-review

  Open Access

  File
  812 Downloads (Pure)

• Therapeutic strategies for spinal muscular atrophy: SMN and beyond

  Bowerman, M., Becker, C. G., Yáñez-Muñoz, R. J., Ning, K., Wood, M. J. A., Gillingwater, T. H., Talbot, K. & UK SMA Research Consortium, 2017, In: Disease Models and Mechanisms. 10, 8, p. 943-954 12 p.

  Research output: Contribution to journal › Review article › peer-review

  Open Access

  File
  98 Downloads (Pure)
• 2016

  Current Progress in Therapeutic Gene Editing for Monogenic Diseases

  Prakash, V., Moore, M. & Yáñez-Muñoz, R. J., Mar 2016, In: Molecular Therapy. 24, 3, p. 465-474 10 p.

  Research output: Contribution to journal › Review article › peer-review

  Open Access

  File
  667 Downloads (Pure)
• 2013

  Lentiviral Vector-Mediated RNA Silencing in the Central Nervous System

  Hutson, T. H., Foster, E., Moon, L. D. F. & Yáñez-Muñoz, R. J., 1 Nov 2013, In: Human Gene Therapy. Methods.

  Research output: Contribution to journal › Review article › peer-review